​ Conditions: Chronic Granulomatous Disease (CGD)

Interventions: Drug: Busulfan; Drug: Tocilizumab; Drug: Eltrombopag; Drug: Sirolimus; Other: pCCLChimGp91lentiviral vector containing the human gp91 phox (CYBB) gene

Sponsors: National Institute of Allergy and Infectious Diseases (NIAID)

Enrolling by invitation Conditions: Chronic Granulomatous Disease (CGD)
Interventions: Drug: Busulfan; Drug: Tocilizumab; Drug: Eltrombopag; Drug: Sirolimus; Other: pCCLChimGp91lentiviral vector containing the human gp91 phox (CYBB) gene
Sponsors: National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation